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News & Updates

2017 Rare Disease Day theme is announced

The theme is “research” and the slogan is “with research possibilities are limitless”. 

 

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Ultragenyx Announces

Withdrawal of Marketing Authorization Application for Aceneuramic Acid Prolonged Release (Ace-ER) in the European Union.


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Upcoming Events

Rare Disease Day

Being observed with number of activities around the World. For an activity near your area. Please see

 


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24-Mar-17

22nd Meeting of the World Muscle Society

is going to be held on 3-7 October, 2017 at St. Malo, France. Treatment of neuromuscular disorders is one of the areas that will be discussed.


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16-Mar-17