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Living with GNE Myopathy

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News & Updates

Challenges faced by people with rare diseases

Challenges faced by people with rare diseases

have been highlighted in a recent newspaper coverage

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Interview of Prof. MadhulikaKabra,

All India Institute of Medical Sciences, New Delhi highlighting the need for pharma companies to participate in drug development for treatment of rare diseases.

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Upcoming Events

22nd Meeting of the World Muscle Society

is going to be held on 3-7 October, 2017 at St. Malo, France. Treatment of neuromuscular disorders is one of the areas that will be discussed.


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16-Mar-17